Overview
Scientists are pursuing gene therapy as a potential medical treatment for some inherited metabolic disorders. Describe the major vector options for gene therapies. In your opinion, which option would be most effective for metabolic disorders such as PKU? Use data and statistics and cite papers to support your argument. (No required format for bibliography, but Endnote is encouraged.)
Gene therapy is accompanied by negative aspects as well. List and describe three possible adverse consequences of gene therapy for metabolic disorders. Be descriptive – use data, statistics, and citations whenever possible.